Rare Disease

Orphan Drugs Treatment for Rare Diseases

Drugs that are evolved specifically to treat rare diseases – called “orphan drugs” – often remain economically of Rare Disease Day, it’s worth reanalyse a series of Healthcare Triage videos we updated last year that majorly focuses on orphan drugs, what’s wrong with the undergoing system, and how we might get ridge out of it. Can we people come out of this undergoing worst system situation? An orphan drug is usually defined as that one used to treat orphan diseases for example heam arginate and many more. 

• Acute intermittent porphyria
• Variegate porphyria
• Hereditary coproporphyria
• Haem arginate